The new MRC CoRE in Therapeutic Genomics aims to transform the diagnosis and treatment of genetic disorders by enabling the mass development of cutting-edge genetic therapies.
They aim to develop therapies for many devastating genetic disorders that are currently untreatable, such as:
– rare disorders that cause severe seizures in infants and neurodevelopmental delay
– certain types of blindness and immune disorders
– severe neurological disorders such as Huntington’s disease
